Wednesday 21 November 2018

Gene Therapy: New horizons for pharmaceutical research


When I began to study in the Pharmacy School, I had read about gene therapy. The world began to know the news about the results of the Human Genome Project, and it was announced centuries of new pharmacological discoveries.

 
Do you can imagine it? Many genetics desease can be cured with a specific treatment. In fact it was posible for many kind of genetics disorders like several types of cáncer, cystic fibrosis and even AIDS.



Gene therapy is an experimental technique that uses genes to treat or prevent disease. In the future, this technique may allow doctors to treat a disorder by inserting a gene into a patient’s cells instead of using drugs or surgery. Researchers are testing several approaches to gene therapy, including:

·    1 Inactivating, or “knocking out,” a mutated gene that is functioning improperly.
·    2. Introducing a new gene into the body to help fight a disease.
3    3. Replacing a mutated gene that causes disease with a healthy copy of the gene.



Although gene therapy is a promising treatment option for a number of diseases (including inherited disorders, some types of cancer, and certain viral infections), the technique remains risky and is still under study to make sure that it will be safe and effective.
So, the future pharmacist have here a big matter to study. I really think this is the future of new kind of personalized medicine, and we can see soon big discoveries about treatment of, until now, incurable deseases.

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